After a rainy morning, the skies cleared enough for over 150 supporters of DART to walk the 2-mile plus course around Tod’s Point in Old Greenwich to raise much needed funds for NPC research. Joining us this year was a group from The Prospector Theater in Ridgefield, CT where Andrew Marella works every week as …
Announcements
IntraBio Announces Successful NPC Phase III Trial
IntraBio Announces Positive Pivotal Trial Results of IB1001 for the Treatment of Niemann-Pick Disease Type C OXFORD, UK / ACCESSWIRE / June 29, 2023 / IntraBio Inc today announced positive topline results from the pivotal, Phase III IB1001-301 clinical trial (NCT05163288), showing IB1001 significantly improved symptoms, functioning, quality of life, and cognition in pediatric and …
Bloomsbury Genetic Therapies Outlines Pre-Clinical Data on CNS Programs including NPC
London, UK, 18 May 2023 – Bloomsbury Genetic Therapies Limited, a clinical-stage biotechnology company developing potentially curative treatments for patients suffering from rare neurological and metabolic diseases based on clinically proven gene therapy technologies, announced today that pre-clinical data from two of its brain-targeted programs, BGT-INAD and BGT-NPC for the treatment of Infantile Neuroaxonal Dystrophy …