Researchers from St. Louis Children’s Hospital at Washington University School of Medicine are enrolling infants 0-6 months with diagnosed NPC disease and evidence of liver disease. The purpose of the study is to learn how well adrabetadex can reduce liver damage in infants diagnosed with NPC disease. The study has an initial 6-week phase during …
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2023 DART To The Finish charity walk raises over $150,000 for NPC research!
After a rainy morning, the skies cleared enough for over 150 supporters of DART to walk the 2-mile plus course around Tod’s Point in Old Greenwich to raise much needed funds for NPC research. Joining us this year was a group from The Prospector Theater in Ridgefield, CT where Andrew Marella works every week as …