by adminDecember 30, 2021May 24, 2023 On December 27, 2021 the Dr. Oz Show featured two families dealing with “Baby Alzheimer’s;” one with a child with Niemann-Pick disease type A and the other with Niemann-Pick disease type C.
DART News Niemann-Pick Type C News Research NewsDART and SOAR-NPC Researcher Dr. Charles Vite in the University of Pennsylvania News! February 18, 2013February 19, 2013
Announcements Niemann-Pick Type C News Research NewsBloomsbury Genetic Therapies Outlines Pre-Clinical Data on CNS Programs including NPC May 24, 2023August 23, 2023
Announcements Niemann-Pick Type C News Research NewsIV Adrabetadex (cyclodextrin) Trial for Neonatal Liver Disease Started October 31, 2023February 27, 2024