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KemPharm to acquire Orphazyme and pursue FDA approval for Arimoclomol

Arimoclomol treatment. On May 15, 2022, KemPharm, Inc., a specialty pharmaceutical company focused on rare central nervous system diseases like NPC, announced its acquisition from Orphazyme of Arimoclomol. This action supports the confidence of NPC clinicians in the benefit of Arimoclomol. “We believe the efficacy signal for Arimoclomol in NPC is convincing and that there …

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DART To The Finish Charity Walk for NPC 2022 – Saturday * Sept. 24, 2022 * 8:00a

Gather your friends and family and join us for this year’s invigorating  2.0 mile walk around beautiful Tod’s Point in Old Greenwich, and help us raise much needed funds to find a cure for Niemann-Pick type C disease. No beach pass, no problem, DART has you covered. We’re expecting a wondrful in-person event, but if …