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NIH and biotech Apertura Gene Therapy collaborate on next-generation AAV delivery of gene therapy for NPC

July 9, 2026 Apertura Gene Therapy Announces Cooperative Research and Development Agreement with Institutes of the NIH to Test Investigational Gene Therapy for Niemann-Pick Disease Type C1  — Cooperative Research and Development Agreement (CRADA) will utilize Apertura’s TfR1 CapX™ Capsid — — Ara Parseghian Medical Research Fund, a non-profit organization dedicated to finding a treatment …