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WALL STREET JOURNAL REPORTS ON NEW NP-C DRUG TRIAL AT THE NATIONAL INSTITUTES OF HEALTH

Read about the detailed efforts of the Marellas and other NP-C families to bring the latest and most promising therapy for NP-C, Cyclodextrin, into an FDA approved clinical trial in an amazing, online experience! Trials: A Desperate Fight to Save Kids & Change Science. For six years, Wall Street Journal reporter Amy Dockser Marcus followed …