Announcements Niemann-Pick Type C News Research NewsAzafaros announces completion of Phase 2 RAINBOW study evaluating nizubaglustat in NPC and other rare disease patients March 13, 2024July 16, 2024
Announcements Banner News Niemann-Pick Type C News Research NewsFDA Approves 2nd New Drug to Treat NPC October 1, 2024October 1, 2024
Announcements DART News Niemann-Pick Type C News Research NewsCyclodextrin Drug Trial Update November 14, 2012February 18, 2013