Announcements Benefit Concert DART News Upcoming DART EventsTHE BEACH BOYS to perform for DART! December 22, 2012June 19, 2013
Announcements Banner News Niemann-Pick Type C News Research NewsMandos Submits New Drug Application to U.S. FDA for Adrabetadex in Infantile-Onset NPC! December 19, 2025December 19, 2025
DART News Niemann-Pick Type C News Research NewsNPC drug Miglustat improves swallowing in children and adolescents with Niemann-Pick type C1 disease September 11, 2020September 11, 2020