by adminDecember 30, 2021May 24, 2023 On December 27, 2021 the Dr. Oz Show featured two families dealing with “Baby Alzheimer’s;” one with a child with Niemann-Pick disease type A and the other with Niemann-Pick disease type C.
Niemann-Pick Type C News Research NewsBloomsbury Genetic Therapies Receives Rare Pediatric Disease Designation from FDA for Gene Therapy Treatment of NPC August 23, 2023February 25, 2025
Announcements Niemann-Pick Type C NewsIntraBio Announces Successful NPC Phase III Trial June 30, 2023January 31, 2024
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