Announcements Niemann-Pick Type C News Research NewsAzafaros Announces IRB approval of 1st Site in U.S. for Phase 2 RAINBOW Study NPC and GM2 May 23, 2023December 15, 2023
Announcements DART News Niemann-Pick Type C News Research NewsNPC Cyclodextrin Clinical Trial to Start! January 12, 2013February 18, 2013
Announcements Benefit Concert DART News Past DART EventsHunter Hayes Gala and Concert Raises $325,000! December 24, 2017April 12, 2018