Announcements Niemann-Pick Type C News Research NewsIntraBio files New Drug Application for N-acetyl-L-leucine (IB1001) for the treatment of NPC January 31, 2024October 1, 2024
Announcements Niemann-Pick Type C News Research NewsAzafaros Announces IRB approval of 1st Site in U.S. for Phase 2 RAINBOW Study NPC and GM2 May 23, 2023December 15, 2023
DART News Niemann-Pick Type C News Research NewsNPC drug Miglustat improves swallowing in children and adolescents with Niemann-Pick type C1 disease September 11, 2020September 11, 2020
