NPC drug Miglustat improves swallowing in children and adolescents with Niemann-Pick type C1 disease

Wonderful scientific confirmation of the benefit for kids from our NPC community’s research efforts! Andrew has been on this medicine since 2004, and our toolbox is just starting to grow!

genetic

Read the article:

https://medicalxpress.com/news/2020-09-miglustat-swallowing-children-adolescents-niemann-pick.html

 

Posted in DART News, Niemann-Pick Type C News, Research News