Announcements DART News DART Walk/RunDART To The Finish Charity Walk for NPC 2022 – Saturday * Sept. 24, 2022 * 8:00a April 10, 2022October 10, 2022
Announcements Niemann-Pick Type C News Research NewsIV Adrabetadex (cyclodextrin) Trial for Neonatal Liver Disease Started October 31, 2023February 27, 2024
Announcements Banner News Niemann-Pick Type C News Research NewsFDA Approves 2nd New Drug to Treat NPC October 1, 2024October 1, 2024