Announcements Niemann-Pick Type C News Research NewsIV Adrabetadex (cyclodextrin) Trial for Neonatal Liver Disease Started October 31, 2023February 27, 2024
Announcements DART News Niemann-Pick Type C News Research NewsMontefiore Einstein Doctor Receives NIH Grant to Expand Newborn Screening and Improve Diagnosis and Access to Treatment October 10, 2019October 10, 2019